• Gene therapy trials treat inherited blindness and deafness

    From JAB@21:1/5 to All on Sat May 11 21:04:15 2024
    XPost: sci.misc

    Gene therapy trials treat inherited blindness and deafness


    Scientists have restored vision and hearing in people born with
    congenital blindness or deafness in two separate gene therapy trials

    https://www.dw.com/en/gene-therapy-trials-treat-inherited-blindness-and-deafness/a-69006407

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  • From D@21:1/5 to JAB on Sun May 12 12:58:47 2024
    XPost: sci.misc

    On Sat, 11 May 2024, JAB wrote:

    Gene therapy trials treat inherited blindness and deafness


    Scientists have restored vision and hearing in people born with
    congenital blindness or deafness in two separate gene therapy trials

    https://www.dw.com/en/gene-therapy-trials-treat-inherited-blindness-and-deafness/a-69006407


    I wonder when we'll see gene therapy treatments to improve human
    functioning above a healthy baseline, instead of just treating deceases?

    Also, with gene therapy, don't you have to "refill" every couple of years?
    Of course that's a massive improvement over taking medication daily, and depending on the treatment, maybe you don't have to, but I have a vague
    memory reading somewhere that the gene therapy results get "flushed out"
    of the system when cells die and your "original" ones are use to replace
    them.

    Not a scientist so caveat emptor as always! ;)

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  • From JAB@21:1/5 to nospam@example.net on Sun May 12 19:53:24 2024
    XPost: sci.misc

    On Sun, 12 May 2024 12:58:47 +0200, D <nospam@example.net> wrote:

    gene therapy treatments

    It's called "gene therapy trials," not gene therapy treatment.

    So, this is essential "let's see what happens" research.

    Medicine has come a long way since 1950, but has not crossed the
    finished line. There is still too much statistical "research"
    happening.

    Some people can do this without consequences, but others cannot.
    Researchers can say statistically, this affects X percent, but they
    can't nail down the specifics as to why.

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  • From D@21:1/5 to JAB on Mon May 13 11:54:22 2024
    XPost: sci.misc

    On Sun, 12 May 2024, JAB wrote:

    On Sun, 12 May 2024 12:58:47 +0200, D <nospam@example.net> wrote:

    gene therapy treatments

    It's called "gene therapy trials," not gene therapy treatment.

    So, this is essential "let's see what happens" research.

    Medicine has come a long way since 1950, but has not crossed the
    finished line. There is still too much statistical "research"
    happening.

    Some people can do this without consequences, but others cannot.
    Researchers can say statistically, this affects X percent, but they
    can't nail down the specifics as to why.


    I think there is at least one gene therapy treatment in production. I read about it at least half a year ago in the mainstream newspaper, but can't remember the details. That was in sweden and it was some where niche
    decease.

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  • From JAB@21:1/5 to nospam@example.net on Mon May 13 06:46:51 2024
    XPost: sci.misc

    On Mon, 13 May 2024 11:54:22 +0200, D <nospam@example.net> wrote:

    gene therapy treatment

    What is gene therapy used to treat?

    Gene therapy aims to fix a faulty gene or replace it with a healthy
    gene to try to cure disease or make the body better able to fight
    disease. It holds promise as a treatment for a wide range of diseases,
    such as cancer, cystic fibrosis, heart disease, diabetes, hemophilia
    and AIDS.

    The U.S. Food and Drug Administration (FDA) has approved gene therapy
    products for several conditions, including cancer, spinal muscular
    atrophy, hemophilia and sickle cell disease. But for most people, gene
    therapy is available only as part of a clinical trial.


    https://www.mayoclinic.org/tests-procedures/gene-therapy/about/pac-20384619

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